Rare Bleeding Disorders

Through evolution, a complex chain reaction has been developed and it is continuously activated in response to bleeding injury, this is called coagulation cascade.

Any deficit or abnormality in the synthesis of a each single coagulation factor in this chain can trigger a bleeding tendency, posing immediate risks and long-term complications.

Without adequate and timely treatment -even prophylaxis in the severe cases- patients can experience acute bleeding either spontaneously in response to trauma or surgery. That can be life threatening (such as intracranial bleeding) or can cause chronic joint damage, anemia, iron deficiency.

Out of numerous coagulation disease, only a few currently have broad access to effective, convenient and accessible treatment Making these unserved patients treated effectively and convenient is today a reachable goal.